World Orphan Drug Congress USA 2026 is a conference and exhibition for the orphan drug and rare disease community, bringing together pharmaceutical and biotechnology companies, regulators, patient advocates, payers, investors and solution providers.

The programme covers drug development, clinical and regulatory strategy, patient data, market access, pricing and reimbursement, cell and gene therapies, AI and digital health, rare oncology and rare disease advocacy, with workshops, exhibition stands, 1-to-1 meetings and innovation showcases.

The 2026 edition is held at the Thomas M. Menino Convention & Exhibition Center in Boston, with 2,000+ attendees and 280+ speakers for companies and organizations working across rare disease therapies and patient access.